Neuroendocrine and small-cell prostate cancer
Neuroendocrine prostate cancer is a form that has stopped depending on the androgen receptor, either from the start or after years of hormone therapy. It no longer shows up on PSA, spreads to the liver and brain, and is treated with the platinum chemotherapy used for small-cell lung cancer.
Overview
Neuroendocrine prostate cancer includes rare de novo small-cell carcinoma and, far more often, treatment-emergent disease that arises when adenocarcinoma under prolonged androgen receptor blockade switches lineage, typically with combined loss of RB1 and TP53, PTEN loss, MYCN or AURKA amplification and loss of androgen receptor and PSA expression. It is suspected when disease progresses with a low or flat PSA, visceral or lytic bone metastases, raised chromogranin, neuron-specific enolase or lactate dehydrogenase, or FDG-avid but PSMA-negative lesions, and confirmed by biopsy showing small-cell morphology or synaptophysin and chromogranin staining. There is no approved therapy specific to it: platinum with etoposide, or carboplatin with docetaxel for mixed histology, is standard, with response rates of about half but brief duration, and androgen deprivation is usually continued. Immunotherapy adds little outside mismatch repair deficiency. DLL3 is expressed in most neuroendocrine prostate cancers, and the DLL3 T-cell engager tarlatamab, approved for small-cell lung cancer, is in trials here; EZH2 inhibitors and aurora kinase inhibitors are being tested against the lineage switch itself.
State of the art
- Sequencing has shown that neuroendocrine prostate cancer evolves from the same clone as the adenocarcinoma rather than arising anew.
- DLL3 gives the disease its first surface target, borrowed from small-cell lung cancer.
Show survival figures (1)
Averages across everyone diagnosed, often years ago. Your stage, subtype, age, fitness and the treatment you receive matter more than the average, and the numbers are improving quickly.
- Lineage plasticity is now studied as a drug target in its own right.
Anatomy and lymph node drainage
- Peripheral zone (most indications)
- Transition zone (BPH)
- Ducts (ductal, intraductal, neuroendocrine)
- Seminal vesicle (T3b)
- Nodes: obturator
- Nodes: internal iliac
- Nodes: external iliac
- Nodes: presacral
About three quarters of indications arise in the peripheral zone at the back of the gland, the part a finger or a biopsy needle reaches; drainage is to the obturator and iliac nodes.
- Peripheral zone (most indications)Mixed adenocarcinoma and neuroendocrine carcinoma
- Transition zone (BPH)
- Ducts (ductal, intraductal, neuroendocrine)Treatment-emergent neuroendocrine prostate cancer (after androgen receptor pathway inhibitors) · Mixed adenocarcinoma and neuroendocrine carcinoma · Large-cell neuroendocrine carcinoma of the prostate
- Seminal vesicle (T3b)
- obturator
- internal iliac
- external iliac
- presacral
Same organ: Prostate cancer, Localised prostate cancer, high and very high risk, Biochemical recurrence of prostate cancer, Metastatic hormone-sensitive prostate cancer, Non-metastatic castration-resistant prostate cancer, Metastatic castration-resistant prostate cancer
Show survival figures (1)
Averages across everyone diagnosed, often years ago. Your stage, subtype, age, fitness and the treatment you receive matter more than the average, and the numbers are improving quickly.
- Pure small-cell prostate cancer is under 1 percent of new diagnoses, but neuroendocrine features emerge in 10 to 20 percent of men treated with potent androgen receptor inhibitors; median survival after diagnosis is about a year.
Cisplatin or carboplatin with etoposide, as for small-cell lung cancer; continue androgen deprivation; brain imaging.
Carboplatin plus docetaxel or cabazitaxel, then platinum with etoposide; clinical trial enrolment preferred.
Biopsy any progression with low PSA, visceral metastases or PSMA-negative FDG-avid lesions; test for mismatch repair deficiency (pembrolizumab) and HRR genes.
DLL3 T-cell engagers (tarlatamab), EZH2 inhibitors and aurora kinase inhibitors against the lineage switch; lurbinectedin borrowed from small-cell lung cancer.
Subtypes & biomarkers
top- De novo small-cell carcinoma of the prostate
- Treatment-emergent neuroendocrine prostate cancer (after androgen receptor pathway inhibitors)
- Mixed adenocarcinoma and neuroendocrine carcinoma
- Aggressive variant prostate cancer (clinical definition, low PSA, visceral spread)
- Large-cell neuroendocrine carcinoma of the prostate
- Synaptophysin, chromogranin and INSM1 staining
- Loss of androgen receptor and PSA expression
- Combined RB1 and TP53 loss
- MYCN and AURKA amplification
- DLL3 expression
- Serum chromogranin A, neuron-specific enolase and lactate dehydrogenase
- FDG PET-avid, PSMA PET-negative lesions
How often this target appears
- 1977Small-cell carcinoma of the prostate first described
- 2011Beltran finds AURKA and MYCN amplification in neuroendocrine prostate cancer
- 2016Divergent clonal evolution from adenocarcinoma shown by sequencing
- 2017RB1 and TP53 loss drive lineage plasticity in models
- 2018Aggarwal: 17 percent of men on potent hormone therapy have neuroendocrine features at biopsy
- 2024Tarlatamab shows activity against DLL3-positive neuroendocrine prostate cancer
Dated changes read from the records linked to this indication: approvals, regulatory steps, reported trials, guideline versions and milestones. Newest first; no date is inferred.
All 7 changes by month →- 2026-09-17This recordNeuroendocrine and small-cell prostate cancerFacts on this page last checked
When this page itself was last checked or edited.
- 2024MilestoneDLL3Tarlatamab shows activity against DLL3-positive neuroendocrine prostate cancer
A milestone in how this cancer is treated.
- 2018MilestoneNeuroendocrine and small-cell prostate cancerAggarwal: 17 percent of men on potent hormone therapy have neuroendocrine features at biopsy
A milestone in how this cancer is treated.
- 2017MilestoneNeuroendocrine and small-cell prostate cancerRB1 and TP53 loss drive lineage plasticity in models
A milestone in how this cancer is treated.
- 2016MilestoneNeuroendocrine and small-cell prostate cancerDivergent clonal evolution from adenocarcinoma shown by sequencing
A milestone in how this cancer is treated.
- 2011MilestoneNeuroendocrine and small-cell prostate cancerBeltran finds AURKA and MYCN amplification in neuroendocrine prostate cancer
A milestone in how this cancer is treated.
What is in development for Neuroendocrine and small-cell prostate cancer, drawn from the whole corpus: 0 items. Drugs are grouped by the most advanced trial phase they have reached anywhere; approved treatments sit under standard of care. Technologies are the methods being tested for this cancer, trials are the studies recorded here, and ideas are proposals not yet in a trial.
Nothing recorded in development for this cancer yet.
Open problems and what is being done
No approved therapy specific to the disease; every regimen is borrowed from lung cancer.
No blood test reliably detects the lineage switch before it shows on scans.
Whether androgen receptor blockade should be de-escalated to slow the switch.
Trials
topTrials recruiting now
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Direct links plus the targets, companies, and technologies of this cancer's products.
technologies
2targets
2drugs
3companies
1Latest papers
topQuery for this indication: (TITLE:"Neuroendocrine and small-cell prostate cancer" OR ABSTRACT:"Neuroendocrine and small-cell prostate cancer" OR TITLE:"NEPC" OR ABSTRACT:"NEPC" OR TITLE:"Treatment-emergent neuroendocrine prostate cancer" OR ABSTRACT:"Treatment-emergent neuroendocrine prostate cancer" OR TITLE:"t-NEPC" OR ABSTRACT:"t-NEPC" OR TITLE:"Small-cell carcinoma of the prostate" OR ABSTRACT:"Small-cell carcinoma of the prostate" OR TITLE:"Aggressive variant prostate cancer" OR ABSTRACT:"Aggressive variant prostate cancer") AND (treatment OR therapy OR trial OR survival OR diagnosis). Results are unfiltered search hits about Neuroendocrine and small-cell prostate cancer, not a curated reading list.
Similar pages
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